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evolved over time to create

three newer haplotypes

Haplotype 1

that each differ by a few

C

A

T

C

A

T

nucleotides (red).

Haplotype 2

T

A

T

C

A

A

Haplotype 3

T

A

T

C

C

A

Haplotype 4

C

G

T

C

A

T

process can help us develop new strategies for

polymorphisms (abbreviated SNPs and profighting disease.

nounced “snips”).

For example, let’s say that a certain nucleotide

Clues from Variation

in one of your genes is A. In your uncle, however,

Scientists know quite a bit about how cells

the nucleotide in the same place on the same

reshuffle genetic information to create each pergene might be G. You and your uncle have slightly son’s unique genome. But many details are

different versions of that gene. Scientists call the

missing about how this genetic variation condifferent gene versions alleles.

tributes to disease, making for a very active area

If two genes sit right next to each other on a

of research.

chromosome, the SNPs in those genes tend to be

What scientists do know is that most of the

inherited together. This set of neighboring SNPs

human genome is the same in all of us. A little

is called a haplotype (see drawing above).

bit of genetic variation— differences that

Most chromosome regions have only a few,

account for much less than 1 percent of our

common haplotypes among all humans. As it

DNA — gives each of us a unique personality,

turns out, these few haplotypes — in different

appearance and health profile.

combinations in each person — appear to account

The parts of the human genome where the

for most of the variation from person to person

DNA sequences of many individuals vary by a

in a population.

single nucleotide are known as singlenucleotide

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44 National Institute of General Medical Sciences Scientists can use haplotype information

to compare the genes of people affected by a

disease with those of unaffected people. For

example, this approach revealed a genetic variation that substantially increases the risk of agerelated macular degeneration, the leading

cause of severe vision loss in the elderly. Scientists

discovered that a single SNP — one nucleotide in

the 3 billionnucleotide human genome— makes

some people more likely to get this eye disease.

The discovery paves the way for better diagnostic

tests and treatments.

What about other diseases? In 2007, an

international scientific team completed a catalog

environments. He’s also curious about whether

of common human haplotypes. Since then,

it can create problems for some individuals.

researchers have been using the catalog to identify

You might be surprised to learn that

genes associated with susceptibility to many com

Rieseberg’s principal research subject is the sunmon diseases, including asthma, diabetes, cancer flower. Although many plants produce only one

and heart disease.

generation a year, plants like sunflowers can be

But not all SNPs are in genes. Scientists studyvery useful tools for researchers asking fundaing genetic variation have also found SNPs in mental questions about genetics. Because their

DNA that doesn’t encode proteins. Nonetheless,

genetic material is more malleable than that of

some of these SNPs appear to affect gene activity.

many animals, plants are excellent models for

Some researchers suspect that the “cryptic”

studying how evolution works.

(hidden) variation associated with SNPs in

Wild sunflowers appealed to Rieseberg

noncoding DNA plays an important role in

because there are several species that live in

determining the physical characteristics and

different habitats. Two ancient species of wild

behaviors of an organism.

sunflowers grow in moderate climates and are

Loren Rieseberg of Indiana University in

broadly distributed throughout the central and

Bloomington is one scientist who would love

western United States.

to take the mystery out of cryptic variation. He

Three recently evolved sunflower species live

wants to know how this noncoding genetic

in more specialized environments: One of the

variation can help organisms adapt to new

new species grows on sand dunes, another grows

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The New Genetics I Life’s Genetic Tree 45

in dry desert soil and the third species grows in

But when Rieseberg looked at the genomes

a salt marsh.

of his hybrid sunflowers, he was surprised to

To see how quickly new plant species could

find that they were just cutandpasted versions

evolve, Rieseberg forced the two ancient sunflowof the ancient sunflower species’ genomes: ers to interbreed with each other, something

large chunks had been

plants but not other organisms can do. Among

moved rather than many

the hybrid progeny were sunflowers that were just

new SNPs created.

like the three recently evolved species! What that

Rieseberg reasons

means is that Rieseberg had stimulated evolution

that plants stash away

in his lab, similar to what actually happened in

unused genetic material,

nature some 60,000 to 200,000 years ago, when

giving them a ready supply of

the newer species first arose.

ingredients they can use to adapt

That Rieseberg could do this is pretty amazquickly to a new environment. It may be that ing, but the really interesting part is how it

human genomes can recycle unused genetic

happened. Scientists generally assume that, for a

material to confront new challenges, as well.

new species with very different characteristics to

evolve, a lot of new mutations have to occur.

Plants like these sunflowers

make great models for studying how evolution works.

ALISON

DAVIS

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46 National Institute of General Medical Sciences 1

2

Living

REX L. CHISHOLM

Laboratories

Like most people, you probably think of fruit flies

Below is a sampling of the wide variety of

as kitchen nuisances. But did you know that sciliving laboratories that scientists are using to entists use these organisms for medical research?

advance human health.

Fruit flies and other model organisms — as

1 Escherichia coli: Bacterium different as mice, plants and zebrafish — permit

“Once we understand the biology of Escherichia scientists to investigate questions that would not

coli, we will understand the biology of an ele

be possible to study in any other way. These

phant.” So said Jacques Monod, a French scientist living systems are, relatively speaking, simple,

who won the 1965 Nobel Prize in physiology or

inexpensive and easy to work with.

medicine for his work on gene regulation. Monod

Model organisms are indispensable to science

was an early proponent of the value of experibecause creatures that appear very different from menting with simple organisms like bacteria. Are

us and from each other actually have a lot in

all bacteria bad? If all you’ve ever heard about E.

common when it comes to body chemistry. Even

coli is its notorious link to tainted hamburger

organisms that don’t have a body—mold and

meat, you may not realize that nondiseasecausing

yeast, for example—can give scientists clues to

strains of the bacterium live in the intestinal tracts

the workings of the tissues and organs of people.

of humans and other animals, helping them in a

This is because all living things process the

variety of ways. For one thing, these bacteria are

nutrients they consume into the same chemicals,

a main source of vitamin K and Bcomplex

more or less. The genes for the enzymes involved

vitamins. They also aid digestion and protect

in metabolism are similar in all organisms.

against infection by harmful bacteria.

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The New Genetics I Life’s Genetic Tree 47

3

NAMBOORI B. RAJU

Scientists all over the world have banded

Dicty normally grows as separate, independent

together to sequence different versions of the

cells. However, when food is limited, neighboring

E. coli genome. Among other things, these studies cells pile on top of each other to create a large,

will help distinguish the genetic differences

multicelled structure containing up to 100,000

between bacteria in a healthy human gut and

cells. This blob ambles along like a slug, leaving

those that cause food poisoning.

a trail of slime behind. After migrating to a more

suitable environment, the blob firms up into a

2 Dictyostelium discoideum: Amoeba towerlike structure that disperses spores, each

This microscopic amoeba—100,000 of them

capable of generating a new amoeba. Because of

form a mound as big as a grain of sand—is an

its unusual properties and ability to live alone or

important tool for health studies. Scientists have

in a group, Dicty intrigues researchers who study determined that Dictyostelium discoideum (Dicty) cell division, movement and various aspects of

has somewhere between 8,000 and 10,000 genes,

organ and tissue development.

many of which are close copies of those in people

and animals but are missing in another single

3 Neurospora crassa: Bread Mold celled organism, yeast. Dicty was first discovered Chances are you don’t think of a moldy bread

in the 1930s in a North Carolina forest and has

crust as a potential science experiment, but

since been found in many similar habitats around

thousands of researchers around the world do!

the world.

Neurospora crassa (Neurospora), which is a species of mold that thrives on bread, is a widely

used model organism for genetic research.

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48 National Institute of General Medical Sciences 4

GARY DITTA

5

ALAN WHEALS

Biologists like to use Neurospora because

like yeast because it grows fast, is cheap to feed

it is simple to grow and has features that make

and safe to handle, and its genes are easy to work

it very suitable for answering questions about

with. We know a lot about mammalian genes

how species arise and adapt, as well as how cells

because scientists can easily insert them into yeast

and tissues change their shape in different

and then study how they work and what happens

environments. Since Neurospora produces spores

when they don’t work.

on a 24hour cycle, the organism is also useful

5 Arabidopsis thaliana: Mustard Plant for studying the biological clocks that govern

Researchers who study plant growth often use

sleep, wakefulness and other rhythms of life.

Arabidopsis thaliana (Arabidopsis), a small, 4 Saccharomyces cerevisiae: Yeast flowering plant related to cabbage and mustard.

There are hundreds of different kinds of yeast, but

This organism is appealing to biologists because

Saccharomyces cerevisiae, the one scientists study Arabidopsis has almost all of the same genes as

most often, is an important part of human life

other flowering plants and has relatively little

outside the lab, too. It is the yeast that bakers use

DNA that does not encode proteins, simplifying

to make bread and brewers use for beer.

the study of its genes. Like people and yeast,

Like Neurospora, yeast is actually a fungus—

plants are also eukaryotes. Arabidopsis grows

not a plant, not an animal, but related to both.

quickly, going from seed to mature plant in only

It is also a eukaryote (as is Neurospora)—a

6 weeks — another plus for researchers who study

“higher” organism with an organized, protective

how genes affect biology.

nucleus that holds its chromosomes. Researchers

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The New Genetics I Life’s Genetic Tree 49

6

7

What do you have in common with a mustard

has a lot of genes —more than 19,000 (humans

plant? Plant cells, and parts of plant cells, comhave about 20,000). Decoding the C. elegans municate with each other in much the same way

genome was a huge milestone for biology, since

that human cells do. For that reason, plants are

it was the first animal genome to be sequenced

good models for genetic diseases that affect

completely. Scientists quickly learned that a vast

cell communication.

number of genes in C. elegans are very similar to genes in other organisms, including people.

6 Caenorhabditis elegans: Roundworm Caenorhabditis elegans (C. elegans) is a creature 7 Drosophila melanogaster: Fruit Fly that is a lot smaller than its name! Several of

The fruit fly species most commonly used for

these harmless roundworms would fit on the

research is named Drosophila melanogaster

head of a pin, although their usual habitat is

(Drosophila). A geneticist’s fruit fly is pretty

dirt. In the lab, they live in petri dishes and eat

much the same as the ones that fly around your

bacteria. C. elegans contains just 959 cells, overripe bananas. In the lab, though, some of

almost a third of them forming its nervous

the flies are exposed to damaging chemicals or

system. Researchers know the fate of every one

radiation, which changes the sequence of their

of these cells!

DNA. Researchers allow the flies to mate, then

This worm is particularly prized by biologists

search among the offspring for flies with

because it is transparent, so what goes on in its

abnormalities. The mutant flies are then mated

tiny body is in plain view under a microscope.

to produce more offspring with the abnormality,

But for such a small, simple animal, C. elegans enabling researchers to close in on the defective

genes involved.

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50 National Institute of General Medical Sciences 9

MONTE WESTERFIELD

8

Fruit flies have been a favorite experimental

Many researchers are drawn to zebrafish

organism among geneticists since early in the

because their eggs and embryos are transparent,

20th century. Hundreds of them can live in a

making it possible to watch development unfold.

pintsized milk bottle or even a small vial, and

In a span of 2 to 4 days, zebrafish cells split and

they reproduce so quickly that keeping track

form different parts of the baby fish’s body: eyes,

of a particular gene as it passes through a couple

heart, liver, stomach and so on. Sometimes,

of Drosophila generations takes only about a

researchers will move a cell to another spot to see

month. It’s also relatively easy to create flies with

if it will still go on to form the same part of the

mutations in many genes, enabling scientists to

body or if it will do something different. This

study how the genes work together.

research has taught scientists about a range of

healthrelated matters in people, including birth

8 Danio rerio: Zebrafish defects and the proper development of blood, the

Zebrafish were originally found in slow streams,

heart and the inner ear.

rice paddies and the Ganges River in East India

and Burma. They can also be found in most pet

9 Mus musculus: Mouse stores and are a home aquarium favorite.

The branches of life’s genetic tree that led eventu

Although the fish have been used by some

ally to mice and to human beings split off from

geneticists for research since the early 1970s, in

each other 75 million years ago, back in the

recent years they have become an especially

dinosaur age. But we are both mammals, and we

popular model organism.

share 85 percent of our genes. Because some

mouse diseases are very similar—sometimes

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The New Genetics I Life’s Genetic Tree 51

10

identical—to human diseases, mice are

Although rats are mammals just like mice,

exceptionally valuable for research.

they differ in important ways. Rats are much

Since the late 1980s, researchers have been

bigger than mice, making it easier for scientists

able to engineer mice with missing genes.

to do experiments that involve the brain. For

Scientists make these “knockout” mice to learn

example, rats have taught scientists a lot about

what goes wrong when a particular gene is

substance abuse and addiction, learning, memory

removed. This gives them valuable clues about

and certain neurological diseases. Rats are also

the gene’s normal function. Identifying these

much better models than mice for studying

genes in humans has helped define the molecular

asthma and lung injury. And since, in people, the

basis for many illnesses.

disease arthritis is more common in women,

studying rats makes more sense because female

10 Rattus norvegicus: Rat rats appear to be more susceptible to arthritis

The Norway rat, or lab rat, was the first animal

than male rats. The opposite is true with mice.

domesticated for use in scientific research.

Currently, they make up about onefourth of all

research animals in the United States. Lab rats have

been used for many decades for testing drugs, and

much of what we know about cancercausing

This Living Laboratories section is

molecules was learned in basic research with rats.

available as a poster. To order a free copy,

visit http://publications.nigms.nih.gov/order.

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52 National Institute of General Medical Sciences The Genome Zoo

longer ago than the ancestor of humans and

Scientists often use an image of a tree to depict

chimpanzees, yet we still share hundreds of genes

how all organisms, living and extinct, are related

with bacteria.

to a common ancestor. In this “tree of life,” each

Scientists use the term comparative genomics

branch represents a species, and the forks bet