Rare Diseases and Scientific Inquiry by National Institute of Health. - HTML preview

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• 1 meter stick

Step 5

• 1 rubber band from dish A (nonstretched)

• 1 paper clip

2

• 1 soda can containing about 2 ounces of water (or other

2–3-ounce weight)

Instruct pairs to record in their notebooks

Page 82

• the question they are investigating and

Step 6

• how far down the meter stick the rubber band stretched.

Collect the rubber bands. Give each pair a rubber band from dish B

Page 82

(previously stretched), and instruct pairs to make and record

Step 7

measurements as before.

Ask volunteers to report their conclusions. Did the two rubber bands

Page 83

perform differently and if so, how?

Step 8

3

Explain that the rubber band from dish A (nonstretched) represents

Page 83

normal connective tissue. Ask,

Steps 9 and 10

• “What do you think the rubber band from dish B represents?”

• “How might looser connective tissue affect the body?”

Explain that now they will investigate whether Patrick has a rare

Page 83

disease affecting his connective tissue.

Step 11

4

5

Lesson 3

93

Activity 3: A Common Thread

Estimated time: 50 minutes

Page and Step

Remind students that Patrick’s symptoms involve more than one body

Page 83

system and seem to have connective tissue in common. They will

Step 1

decide which, if any, rare disorder of connective tissue Patrick may

have.

Arrange the class in pairs. Give each pair a copy of Master 3.8 and Page 84

Master 3.9. Instruct students to use information on Master 3.9 to Steps 2-p

complete Master 3.8.

and 3-p

Ask volunteers to report their conclusions.

Page 84

Step 4

Agree that Marfan syndrome best explains for Patrick’s symptoms. Ask,

Page 85

• “What is the cause of Marfan syndrome?”

Step 5

• “What evidence is there to suggest that Patrick may have Marfan

syndrome?”

Explain that students will look on a handout for evidence of Marfan

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syndrome in Patrick’s family and record in their notebooks what they

Step 6-p

find. Give each student pair a copy of Master 3.10.

Remind students of the three major causes of disease. Ask,

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• “Did you find any evidence of Marfan syndrome in Patrick’s family?”

Step 7

• “Is there evidence to suggest that Patrick’s symptoms may have a

different cause?”

Explain that an early diagnosis of Marfan syndrome allows people to

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take steps to protect their health. Ask, “In what ways might having

Step 8

Marfan syndrome affect your life?”

Conclude by explaining that students will now consider how Marfan

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syndrome affects the lives of people who have it. Ask students to write Step 9-p in their notebooks

• one question they would like to ask a doctor about Marfan

syndrome and

• one way they think having Marfan syndrome might affect their lives.

Ask volunteers to report what they wrote.

Page 87

Step 10-p

Display Master 3.11, and give students time to read it. Ask,

Page 88

• “Were the questions and comments from the young people on

Steps11-p

the master similar to yours?”

and 12-p

• “How would you want to be treated by your classmates if you

had Marfan syndrome?’

= Involves making a transparency.

= Involves copying a master.

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Rare Diseases and Scientific Inquiry

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index-101_2.jpg

Lesson 4

The Importance of Medical Research

1

2

Elaborate

At a Glance

Overview

Lesson 4 introduces the idea that medical research is important for the 3

treatment of a rare disease, childhood leukemia. In the first activity, students meet Jason and Kim, parents of a daughter named Hanna,

who has been diagnosed with childhood leukemia. Students perform a

simulated Web search to learn about the disease. They must sift through different Web hits to find relevant and accurate information about the

disease. In considering a genetic cause of the disease, students perform a karyotype analysis on each family member. In the second activity, students are introduced to treatments for leukemia. They design a clinical trial to guide the treatment of the disease. Finally, students watch a brief video (or, for classes using the print version, act out an interview) of a leukemia 4

survivor discussing what it’s like to live with the disease.

Major Concepts

• Much medical information can be found on the Internet; however, this

information must be examined carefully to assess its relevance and

accuracy.

• Lack of appearance in a family history does not mean that a disease

doesn’t have a genetic cause.

• Leukemia is a cancer of the white blood cells.

• Clinical trials have greatly improved the survival rates of children with leukemia.

5

95

Objectives

After completing this lesson, students will

• have used a simulated Web search to learn about the cause, symptoms,

and diagnosis of childhood leukemia;

• have performed a karyotype analysis to diagnose leukemia;

• have designed and tested a clinical trial for treating childhood leukemia; and

• have considered the challenges associated with living with leukemia.

Teacher Background

Consult the following sections in Information about Rare Diseases and

Scientific Inquiry:

2.0 The Impact of Genomics on Rare Diseases (pages 24–27)

3.0 Rare Infectious Diseases (page 26)

4.0 Rare Diseases Caused by Environmental Toxins (pages 27–28)

5.3 Childhood Leukemia (pages 31–33)

In Advance

Web-Based Activities

Activity

Web Component?

1

Yes

2

Yes

Photocopies, Transparencies, Equipment, and Materials

Photocopies and Transparencies

Activity 1: An Unwelcome Diagnosis

For Classes Using the Web-Based Activity:

1 transparency of Master 4.1

1 copy of Masters 4.2 and 4.5 for each student

1 transparency and 1 copy for each student of Master 4.3

1 copy of Master 4.4 for each pair of students

For Classes Using the Print-Based Activity:

1 transparency of Master 4.1

1 copy of Masters 4.2, 4.5, 4.11, and 4.12 for each student

1 transparency and 1 copy for each student of Master 4.3

1 copy of Masters 4.4 and 4.10 for each pair of students

Continued

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Rare Diseases and Scientific Inquiry

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Photocopies and Transparencies

Activity 2: Clinical Trials

For Classes Using the Web-Based Activity

1 transparency of Master 4.6

1 copy of Masters 4.7, 4.8, and 4.9 for each pair of students

1

For Classes Using the Print-Based Activity:

1 transparency of Master 4.6

1 copy of Masters 4.7, 4.8, 4.9, 4.13, 4.14, 4.15, and 4.16 for each pair of students

2 copies of Master 4.17 for the class

Equipment and Materials

For Activities 1 and 2, Web-based versions, students will need computers with Internet access.

2

Preparation

Activities 1 and 2

For classes using the Web version, verify that the computer

lab is reserved for your class or that classroom computers

are set up for the activities.

Refer to Using the Web Site for details. Check that the Internet

connection is working properly.

3

Log on to the Web Portion of Student Activities section at

http://science.education.nih.gov/supplements/rarediseases/student

Select “Lesson 4: The Importance of Medical Research.”

Procedure

Note: This is an Elaborate lesson. It gives students an opportunity to take 4

what they have learned about rare diseases and scientific inquiry from

the previous lessons and apply it in a new setting. In the first activity, students place themselves in the role of a parent whose child has just

been diagnosed with childhood leukemia. They perform a simulated Web

search to learn about the disease. This activity is designed to help students hone their skills in evaluating information for relevance and accuracy.

The genetic link to the disease is made real to students by having them perform a simple karyotype analysis.

In the second activity, students exercise their understandings of scientific 5

inquiry in the context of clinical trials. Designing a fair test is a common Lesson 4

97

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inquiry skill. We selected childhood leukemia because it is a rare disease that has a genetic cause. It’s a serious disease, but, at the same time, it represents a real success story in the application of medical research to treatment.

The activity includes a graph that shows how survival rates for children with leukemia have dramatically improved over the past few decades. The lesson concludes with a video (or a role-play) of a young woman who has come through treatment for the disease and is now pursuing a medical

education. The inclusion of this story is designed to give students an

opportunity to empathize with someone who has had leukemia and also to

leave them with the vision of a positive outcome.

Activity 1: An Unwelcome Diagnosis

Estimated time: 100 minutes

1.

Begin the lesson by explaining that students will investigate a

case study involving a child with a rare disease.

This case study introduces the use of clinical trials to obtain

evidence about which treatment options are most effective. It’s

not important that students understand the clinical trials process.

Instead, clinical trials provide a real-life example of how the practice of science (especially proper experimental design) can help improve

people’s health.

2.

Display Master 4.1, Doctor Visits. Ask for volunteers to read aloud each section of text.

3.

Ask students how they would feel if they were Hanna’s parent

and received this disturbing news. Ask, “What would you

Content Standard C:

do now that you have learned that your daughter has been

diagnosed with leukemia?”

Disease is a

breakdown in

Students’ responses will vary. Some students may suggest getting a

structures or functions

second opinion. Others may suggest researching cancer treatment

of an organism. Some

centers. Accept all answers and guide the discussion to the need to

diseases are the result

obtain more information.

of intrinsic failures of

the system. Others are

4.

Explain that although the doctor described childhood

leukemia and answered their questions during the office

the result of damage

visit, Jason and Kim were so upset that they didn’t take notes

by infection by other

or remember much of what they were told. After returning

organisms.

home with Hanna, they performed an Internet search on

leukemia.

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Rare Diseases and Scientific Inquiry

5.

Ask students,

“If you were Hanna’s parent, what information would you

want to have about the disease?”

“Where could you find the information that you want?”

Make a list on the board of the types of information about leukemia

the students request. Students may mention a variety of sources

1

for this information, including their doctors, books, television

programs, the Internet, and, possibly, friends and family who have

had to cope with the disease.

6.

Give each student one copy each of Master 4.2, Internet Search

Results, and Master 4.3, Evaluating Internet Search Results.

Instruct students to view the list of hits on Master 4.2 and

follow the instructions on Master 4.3 to rank the hits from most

helpful to least helpful.

2

This step is designed to challenge students to sort through

information related to leukemia and decide

• which hits are most likely to contain the information they want

and

• which hits are likely to contain information that is accurate and

unbiased.

There is no single correct answer to ranking these eight hits. Rather,

you should see whether students can sift through the lists to identify

one or two of the best hits. Likewise, students should be able to

identify another couple of hits as clearly not helpful to providing the 3

information they want.

In this activity, students are ranking hits based on relevance and

accuracy. There are, however, other criteria that students should

use to assess the usefulness of Web sites. For example, the site

should present information that is up to date, and the information

should be as free of bias as possible, such as the bias associated with promoting a product or service.

Answer key for Web hits on Master 4.2, Internet Search Results

4

1. Federal Center for Cancer Research

Information about leukemia, its causes, symptoms, diagnosis,

and treatment …

Hit 1 is from a fictional U.S. government research organization,

the Federal Center for Cancer Research. The Federal government,

however, does support medical research, primarily through the

5

Lesson 4

99

National Institutes of Health (NIH). For example, the Office of

Rare Diseases Research (http://rarediseases.info.nih.gov/) and the

National Cancer Institute (http://www.cancer.gov/) are parts of

NIH and provide accurate medical information resources for the

general public. Such government sites post information that has

been reviewed by experts and is labeled “no commercial bias,”

which means that the information presented hasn’t been selected to

promote the use of any particular product or service. Such sites are a logical place to begin to learn about a rare disease.

2. My Leukemia Blog

Living with Cancer: Reflections and remembrances of a cancer

survivor …

Personal blogs can provide a window into the life of someone

who has a rare disease. The person may or may not choose to

include medical information as part of the blog. Furthermore, any

medical information on the blog may reflect a possibly incomplete

understanding by the author. Although such blogs can be helpful

resources, they are not the best place to begin to learn about a rare disease.

3. The Cancer Research Center at Lincoln State University

Breast cancer, Prostate cancer, Leukemia, Lymphoma, …

Research centers based at universities often provide medical

information to the public. The information is reviewed by experts

for accuracy. Often, the posted information is tied to the research interests of individual scientists and may be too specific to be a

starting point for searching about a rare disease.

4. Information about Leukemia from the American Blood

Cancer Society

Cells of the blood, Stem cells and leukemia, White blood cells

and bacteria …

Hit 4 is from a patient support group. Although the American Blood

Cancer Foundation is fictional, a large number of patient-support

organizations exist to promote medical research and support for

people with rare diseases. In the case of leukemia, the Leukemia

and Lymphoma Society (http://www.leukemia.org/hm_lls) is a very

useful resource that provides reliable disease information as well as a variety of patient services. Such sites are a logical place to begin to learn about a rare disease.

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5. Leukemia—Medhealthopedia: The Do-It-Yourself Encyclopedia

Leukemia is a form of cancer that is …

Medhealthopedia is a fictional Web site that provides medical

information to the public in a manner similar to Wikipedia. On

such a site, the information posted is written collaboratively by

users of the site. The information is often reliable, but there is

1

no assurance that experts have reviewed it or that it is free of

commercial bias.

6. Cancer drugs for less! Leukemia

Order drugs from overseas to treat leukemia and save!

Hit 6 is included as a reminder that some information about disease on the Internet is more concerned with making money for someone

than with providing objective medical information.

2

7. Fed approves new drug to treat leukemia

Medical Business Weekly (Washington, DC)—The Food and

Drug Administration today approved Hamilton Pharmaceutical’s

As students report

drug Arresta for the treatment of leukemia …

how they ranked

the hits from the

Hit 7 is from a business publication. Although the information is

likely to be accurate, it only describes one specific development in simulated Web

the field of leukemia research and is not a good place to begin to

search, you have

learn about the disease.

an opportunity to

assess how well they

8. Leukemia: Definition from Medical Jargon.com

3

use their critical-

Leukemia—A form of cancer involving the white blood cells.

thinking skills to

White …

evaluate information

Hit 8 comes from a medical dictionary and only provides a brief

for its relevance and

definition of the disease.

accuracy.

7.

Display Master 4.3. Ask for volunteers to report how they

ranked the Web hits.

Students’ responses will vary. Allow several volunteers to report

their rankings with explanations of their reasoning. Remember

4

that the precise ranking of the Web sites is not important. Ideally,

students will recognize that Hits 1 and 4 are the best places to begin

to learn about leukemia. Hits 2, 3, and 5 can also be useful, but the

information may not be as relevant or as accurate as that from Hits

1 and 4. Some students may reason that Hit 8, which provides a

definition, is a good place to start. Hits 1 and 4, however, will also

provide a definition along with a lot of other useful information.

Hits 6 and 7 are clearly not very useful.

5

Lesson 4

101

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In classrooms using the Web version of the activity:

8-w. Arrange the students in pairs. Give each pair

one copy of Master 4.4, Summarizing Information

a