Rare Diseases and Scientific Inquiry by National Institute of Health. - HTML preview

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Activity 2: Clinical Trials

Estimated time: 50 minutes

Page and Step

Display Master 4.6. Ask volunteers to read it aloud.

Page 107

Step 1

1

Explain that doctors compare the effectiveness of cancer

Page 107

treatments by looking at the percentages of patients still alive

Step 2

after five years.

Explain that students will go back to the year 1970 and assume

Page 107

the roles of doctors trying to improve the survival rates of

Step 3

children with leukemia by conducting a clinical trial.

Give each student pair a copy of Master 4.7. Explain that it

Page 107

describes the treatment options they can include in their clinical

Step 4

trial.

2

Explain that student pairs will use computers to design and carry Page 108

out their clinical trial. Explain that

Step 5-w

• The standard therapy is a combination of the standard

doses of drugs A, B, and C.

• Pairs will select drug doses and the use or nonuse of the

central nervous system treatment.

• They will submit the design for approval. Once approved, the

trial will be carried out and students will learn the results.

Give each pair a copy of Master 4.8 . Instruct students to record Page 109

3

their treatment options, trial results, and conclusions on it.

Step 6-w

Explain that in a clinical trial such as this, the experimental

Page 109

treatment is compared with the standard treatment. Ask, “Should Step 7-w the clinical trial also include a group that receives no treatment?”

Direct students to their computers and instruct them to click

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on “Activity 2: Clinical Trials.” Student pairs should select the

Steps 8-w

treatments and then click “Submit.”

and 9-w

• If approved, students can click “Run treatment” and learn

4

the results.

• If rejected, students can redesign the trial.

• After recording the trial results, students should make and

record their conclusions.

Reconvene the class. Ask volunteers to report the designs and

Page 112

results of the trials and how their treatment compared with the

Step 10

standard treatment.

5

Lesson 4

117

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Give each student a copy of Master 4.9 and explain that this is

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what the doctor showed Hanna’s parents to help them see how

Step 11

effective clinical trials have been in improving survival rates of

children with leukemia.

Remind students of the Web search they performed about

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leukemia. Ask, “What other results from the Web search

Step 12

could provide us with a different perspective about childhood

leukemia?”

Conclude the lesson by explaining that students will watch

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a brief video created by a young woman who is a leukemia

Step 13-w

survivor. Ask students to write in their notebooks some

questions they would like to ask the young woman about her

experiences.

Instruct students to click on “Activity 2: Hailey’s Story” and watch Page 113

the video.

Step 14-w

Reconvene the class and ask volunteers to describe their

Page 113

reactions to the video and to explain how it addressed (or did

Step 15-w

not address) the questions they wrote in their notebooks.

= Involves making a transparency.

= Involves copying a master.

= Involves using the Internet.

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Rare Diseases and Scientific Inquiry

Lesson 4 Organizer: Print Version

Activity 1: An Unwelcome Diagnosis

Estimated time: 100 minutes

Page and Step

1

Explain that students will explore a case study of a child who has a

Page 98

rare disease.

Steps 1

• Display Master 4.1.

and 2

• Ask volunteers to read paragraphs aloud to the class.

Ask, “What would you do now that you have learned that your

Page 98

daughter has been diagnosed with leukemia?”

Step 3

Explain that after the upsetting visit to the doctor, Jason and Kim

Page 98

performed an Internet search on leukemia.

Step 4

Ask students:

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2

• “If you were Hanna’s parent, what information would you want to

Step 5

have about the disease?”

• “Where could you find that information?”

Give each student one copy of Masters 4.2 and 4.3. Instruct students Page 99

to rank on Master 4.3 the usefulness of the hits listed on Master 4.2.

Step 6

Display Master 4.3. Ask volunteers to report how they ranked the Web Page 101

hits.

Step 7

Arrange the class in pairs. Give each pair a copy of Masters 4.4 and Page 102

3

4.10. Ask students to read Master 4.10 and summarize the information Steps 8-p

on Master 4.4.

and 9-p

Reconvene the class and ask whether students have questions about

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the information from the Web hits.

Step 10

Remind students about the three general causes of disease. Ask, “What Page 103

types of information would you want to have in order to decide which

Steps 11 and 12

of the three causes of disease applies to leukemia?”

Explain that Jason and Kim have two children: Hanna, who has

Page 103

leukemia, and Rick, her healthy older brother. Also, say that there’s no Steps 13 and 14

4

history of leukemia in the family. Ask,

• “Does this rule out genetics as the cause of leukemia?”

• “What about environmental exposure or infections?”

Acknowledge that so far, there isn’t good evidence to suggest a cause

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for Hanna’s leukemia. Remind students about the Animation about

Step 15

Leukemia. Ask, “What happened to a stem cell that led to leukemia?”

5

Lesson 4

119

Explain that new mutations happen from exposure to sunlight and

Page 103

substances in the environment or from an uncorrected DNA-copying

Step 16

mistake. Mutations in genes associated with cell growth can lead to

cancer.

Explain that mutations can affect the number and appearance of

Page 104

chromosomes and that a photograph of chromosomes under a

Step 17

microscope is a karyotype. Give each student a copy of Master 4.5.

Instruct students to read Master 4.5 and answer the question at the Page 104

bottom. Explain that in leukemia, we expect a karyotype to show

Steps 18 and 19

three, not two, copies of at least one of the numbered (nonsex)

chromosomes.

Explain that students will now view karyotypes from Hanna and her

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immediate family. Ask students to predict whether each karyotype will

Step 20-p

appear normal or abnormal and to record in their notebooks whether

the evidence supports the predictions.

Give each student pair a copy of Master 4.11. Ask them to note

Page 106

whether their predictions were confirmed.

Step 21-p

Explain that students will now look at three different karyotypes from

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Hanna: from her blood, cheek, and hair follicles. Ask pairs to predict

Step 22a-p

how each karyotype will appear and to record their predictions.

Give each student pair a copy of Master 4.12. Ask students to note Page 106

whether their predictions were confirmed.

Step 22b-p

Ask, “How can you account for the appearance of the karyotypes taken

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from these three different tissues?”

Step 23-p

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Rare Diseases and Scientific Inquiry

Activity 2: Clinical Trials

Estimated time: 50 minutes

Page and Step

Display Master 4.6. Ask volunteers to read it aloud.

Page 107

Step 1

1

Explain that doctors compare the effectiveness of cancer treatments by

Page 107

looking at the percentages of patients still alive

Step 2

after five years.

Explain that students will go back to the year 1970 and assume the

Page 107

roles of doctors trying to improve the survival rates of children with

Step 3

leukemia by conducting a clinical trial.

Give each student pair a copy of Master 4.7. Explain that it describes Page 107

the treatment options they can include in their trial.

Step 4

Tell students that they will work in their pairs to design and carry out a Page 110

2

clinical trial. Explain that

Step 5-p

• the standard therapy is a combination of the standard doses of

drugs A, B, and C,

• pairs will select drug doses and the use or nonuse of the central

nervous system treatment, and

• they will submit the design to you for analysis.

Explain that in clinical trials, an experimental treatment is compared

Page 110

with the standard treatment. Ask, “Should the clinical trial also include Step 6-p

a group that receives no treatment?”

3

Give each pair a copy of Master 4.8 . Instruct students to record on it Page 111

the treatment options they select, and then to submit it to you. Explain Steps 7a-p

what an Institutional Review Board is, and check that student designs

and 7b-p

test only one variable.

Once you’ve approved all the clinical trial designs, give each student

Page 111

pair the appropriate handout (Master 4.13, 4.14, 4.15, Step 8-p

or 4.16)

Ask student pairs to summarize the data and their conclusions and

Page 111

reasoning on Master 4.8.

Step 9-p

4

Reconvene the class and ask volunteers to report which treatment they Page 112

used and whether it was better than the standard one.

Step 10

Give each student a copy of Master 4.9 and explain that this is what Page 112

the doctor showed Hanna’s parents to help them see how effective

Step 11

clinical trials have been in improving survival rates of children with

leukemia.

Remind students of the Web search they performed about leukemia.

Page 112

Ask, “What other results from the Web search could give us a different

Step 12

perspective about childhood leukemia?”

5

Lesson 4

121

Acknowledge that blogs and videos by cancer survivors can offer

Page 114

important perspectives on what it’s like to live with that illness.

Step 13-p

Conclude by explaining that the class will conduct a brief interview

with a high school senior who was diagnosed with leukemia in eighth

grade.

Ask for one volunteer to play Hailey and one to play the interviewer,

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give each of them a copy of Master 4.17, and have them conduct the Steps 14-p

interview in front of the class.

and 15-p

Ask volunteers to describe their reactions to the interview.

Page 114

Step 16-p

= Involves making a transparency.

= Involves copying a master.

122

Rare Diseases and Scientific Inquiry

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Lesson 5

Communicating about Rare Diseases

1

2

Evaluate

At a Glance

Overview

Lesson 5 gives students the opportunity to reflect on what they have

3

learned about rare diseases and scientific inquiry during this supplement.

Students role-play staff members of a patient-support organization and

are tasked with creating informational posters for the public about Marfan syndrome and childhood leukemia. After students create the posters, they evaluate another poster for a different disease. Finally, students return to the reality TV show scenario that began the supplement. They revisit their initial ideas about rare disease and their attitudes toward people affected by them. They reexamine their answers to the questions about rare diseases posed in Lesson 1 and discuss how their thinking has changed.

4

Major Concepts

• Diseases have three main causes:

– genetics

– environmental exposure

– infectious agents

• Rare diseases may become common, and common diseases may become

rare.

• Some rare diseases can be cured, while many others can be managed

through treatment.

• People with rare diseases must sometimes cope with the stigma

associated with their condition.

5

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Objectives

After completing this lesson, students will have

• revisited their preconceptions about the nature of disease in light of scientific conceptions,

• summarized information about childhood leukemia and Marfan

syndrome, and

• considered their feelings about people affected by rare diseases.

Teacher Background

Consult the following sections in Information about Rare Diseases and

Scientific Inquiry:

2.0 The Impact of Genomics on Rare Diseases (pages 24–26)

3.0 Rare Infectious Diseases (page 26)

4.0 Rare Diseases Caused by Environmental Toxins (pages 27–28)

5.1 Necrotizing Fasciitis (pages 28–29)

5.2 Marfan Syndrome (pages 29–31)

5.3 Childhood Leukemia (pages 31–33)

In Advance

Web-Based Activities

Activity

Web Component?

1

No

2

Yes

Photocopies, Transparencies, Equipment, and Materials

Photocopies and Transparencies

Activity 1: Creating an Informational Poster

1 transparency and 1 copy of Master 5.1 for each student pair

1 copy of Master 5.2 for each student pair addressing Marfan

syndrome

1 copy of Master 5.3 for each student pair addressing childhood

leukemia

1 transparency and 1 copy for each student pair of Master 5.4

1 copy of Master 5.5 for each student pair

Activity 2: Reflecting on Rare Diseases

For Classes Using the Web-Based Version

1 copy of Master 5.6 for each student

Continued

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Rare Diseases and Scientific Inquiry

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Photocopies and Transparencies

Activity 2: Reflecting on Rare Diseases

For Classes Using the Print-Based Version

1 copy of Master 5.6 for each student

1 transparency of Master 5.7

1

Equipment and Materials

For Activity 1, students will need chart paper and colored marking pens.

For Activity 2, Web-based version, students will need computers with Internet access.

Preparation

Activity 1

Gather chart paper and colored marking pens for each student pair. Make photocopies and transparencies.

2

Activity 2

For classrooms using the Web version, verify that the

computer lab is reserved for your class or that classroom

computers are set up for the activities. Refer to Using the

Web Site for details about the site. Check that the Internet

connection is working properly.

Log on to the Web Portion of Student Activities section of the site at

3

http://science.education.nih.gov/supplements/rarediseases/student

Select “Lesson 5: Communicating about Rare Diseases” so students can

begin the activity right away.

Procedure

Activity 1: Creating an Informational Poster

4

Estimated time: 50 minutes

Note: This is an Evaluate lesson. It’s not designed to teach new content but rather to give you a chance to assess how well students

have learned the major concepts about rare diseases and scientific

inquiry.

1.

Begin by explaining that in this final lesson of the supplement,

students will play the roles of staff members working for an

5

Lesson 5

125

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index-132_2.png

organization that informs and support patients with rare

diseases and their families. Explain the following:

Many rare diseases have support groups that raise awareness

and money to support research about the disease.

The task is for pairs to prepare informational posters that

Content Standard C:

explain important aspects of a rare disease to patients, family

Disease is a

members, and other interested people.

breakdown in

structures of functions

Students may feel unqualified to prepare informational posters

of an organism. Some

about rare diseases. You can explain that the posters will deal with

diseases are the result

the rare diseases they have been studying. Furthermore, the goal

of the poster is to communicate information to the public, so the

of intrinsic failures of

posters should use language that everyone can understand.

the system. Others are

the result of damage

2.

Arrange students into pairs again. Explain that each pair will

by infection by other

create a poster about childhood leukemia or Marfan syndrome.

organisms.

Assign half of the pairs to childhood leukemia and the other

half to Marfan syndrome. Explain that after each pair creates a

poster, they will evaluate a poster about the other rare disease.

You may allow student pairs to select the disease they prefer. If

selections heavily favor one disease over the other, you may need to

instruct some pairs to switch diseases to maintain a balance between

the two.

Tip from the field test: If your classroom has the

technical capacity, consider allowing students to create

a PowerPoint presentation instead of a poster.

3.

Display Master 5.1, Guidelines for the Poster, and give each pair a copy to use as a reference. Explain that the handout lists

Content Standard A:

the types of information that should be in the poster. Briefly

Students should base

go over the items on the handout and answer any questions

their explanations on

students have.

what they observed,

and as they develop

Make sure that students have access to the notebooks that contain

cognitive skills,

their work from previous lessons. This work will help students

complete the first part of the poster.

they should be

able to differentiate

Note: The purpose of this activity is to assess students’ learning from the explanation from

previous lessons. Therefore, do not allow students to conduct a research description—proving

project using the Internet or other outside resources.

causes for effects

and establishing

4.

Explain that the second part of the poster will contain a brief

summary of a recent clinical trial or research study about the

relationships based